Antisense Oligonucleotide Therapy for the Nervous System: From Bench to Bedside with Emphasis on Pediatric Neurology.

By Michael Foley|2022-12-15T15:06:26+00:00November 5, 2022|Comments Off on Antisense Oligonucleotide Therapy for the Nervous System: From Bench to Bedside with Emphasis on Pediatric Neurology.

Read More

Patients’ view on gene therapy development for lysosomal storage disorders: a qualitative study.

By Michael Foley|2022-12-15T15:07:01+00:00October 21, 2022|Comments Off on Patients’ view on gene therapy development for lysosomal storage disorders: a qualitative study.

Read More

CNS-Targeting Therapies for Lysosomal Storage Diseases: Current Advances and Challenges.

By Michael Foley|2022-12-15T15:04:40+00:00November 12, 2020|Comments Off on CNS-Targeting Therapies for Lysosomal Storage Diseases: Current Advances and Challenges.

Read More

Current and Future Prospects for Gene Therapy for Rare Genetic Diseases Affecting the Brain and Spinal Cord.

By Michael Foley|2022-12-15T15:08:19+00:00October 6, 2020|Comments Off on Current and Future Prospects for Gene Therapy for Rare Genetic Diseases Affecting the Brain and Spinal Cord.

Read More

Gene Therapy for Neurodegenerative Diseases: Slowing Down the Ticking Clock.

By Michael Foley|2022-12-15T15:07:40+00:00September 18, 2020|Comments Off on Gene Therapy for Neurodegenerative Diseases: Slowing Down the Ticking Clock.

Read More

Families and Researchers Collaborate in Advancing Therapy: The Role of NTSAD, Together with Parents, in Driving Toward Treatments.

By Michael Foley|2022-12-15T15:05:43+00:00February 28, 2017|Comments Off on Families and Researchers Collaborate in Advancing Therapy: The Role of NTSAD, Together with Parents, in Driving Toward Treatments.

Read More