Leading the worldwide fight to treat and cure
Tay-Sachs, Canavan, GM1 and Sandhoff diseases

NTSAD Virtual Family Conference | 2021 Canavan Research Breakout

David Pleasure, MD
Canavan Antisense Therapy

Dominic Gessler, MD
UMass Medical Center
Canavan Research Update

The video recording containing Dr. Gessler's slides cannot be publicly shared at this time. Listen to the audio recording of his presentation here.

Kathleen Kirby, Mike Kiefer, DPT, and Jenny Laforet, MD, PhD
Aspa Therapeutics
CANinform: Canavan natural history study
CANinspire: Aspa Therapeutic gene therapy trial

Paola Leone, PhD
CureRareDisease, LLC
Canavan Gene Therapy, Dayton Children's Hospital

Virtual Conference

View the NTSAD Annual Family Conference Research Exhibit Hall

Please contact Becky Benson, Conference and Family Services Coordinator here with any questions or concerns that are conference related.

2021 Conference Sponsors

Laura and Simeon Schindelman
Bonnie and Barry Davis in loving memory of Adam Davis 
The Evan Lee Ungerleider Fund
NTSAD New York Area Fund 
*sponsors as of 4/15/21