Leading the worldwide fight to treat and cure
Tay-Sachs, Canavan, GM1 and Sandhoff diseases

NTSAD Virtual Family Conference | 2021 Late Onset GM2 Research Breakout

Steve Walkley, PhD, Albert Einstein College of Medicine
LOTS Think Tank

Heather Gray-Edwards, PhD, UMass Medical School
Gene therapy studies in sheep

Camilo Toro, MD, NIH
Medications Do’s and Don’ts

Heather Lau, MD
Questions to ask your doctor about Clinical Trials

Taylor Fields, Senior VP
IntraBio clinical trial

Isabela A Batsu, MD, Global Project Head, Rare Disease and Rare Blood Disorder Development
Sanofi Genzyme: Late Onset GM2 Patient Journey poster


Virtual Conference

View the NTSAD Annual Family Conference Research Exhibit Hall

Please contact Becky Benson, Conference and Family Services Coordinator here with any questions or concerns that are conference related.

2021 Conference Sponsors

Laura and Simeon Schindelman
Bonnie and Barry Davis in loving memory of Adam Davis 
The Evan Lee Ungerleider Fund
NTSAD New York Area Fund 
*sponsors as of 4/15/21