Leading the Fight to treat and cure
Tay-Sachs, Canavan, Sandhoff, GM1 and related diseases

Tay Sachs, Sandhoff, GM1, Fabry, Gaucher, Niemann-Pick, Pompe are lysosomal storage disorders. Tay Sachs and Sandhoff are both categorized as GM-2 gangliosidoses. This is because they are both caused by the build up of GM-2 gangliosides, as described below.

 

*Pompe is also a glycogen storage disorder.

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