Leading the worldwide fight to treat and cure
Tay-Sachs, Canavan, GM1 and Sandhoff diseases

  • Imagine & Believe

    Imagine & Believe

    Join industry leaders and supporters in honoring NTSAD families everywhere during our live, virtual Imagine & Believe event on November 10th, 4:30-5:30 p.m. EST. Free to attend. Donations welcome.

  • 1

Latest News

  • 1
  • 2
  • 3

Tay Sachs, Sandhoff, GM1, Fabry, Gaucher, Niemann-Pick, Pompe are lysosomal storage disorders. Tay Sachs and Sandhoff are both categorized as GM-2 gangliosidoses. This is because they are both caused by the build up of GM-2 gangliosides, as described below.


*Pompe is also a glycogen storage disorder.