NTSAD Research: Developing Treatments, Therapies, and a Cure

Research to Advance Understanding, Inform Treatment, and Improve Quality of Life

The National Tay-Sachs & Allied Diseases Association (NTSAD) is dedicated to finding effective treatments and – ultimately – a cure for Tay-Sachs, Canavan, GM1, and Sandhoff diseases.

Working with our leadership, we drive research, forge collaboration, and foster community among researchers around the world. NTSAD research is informed by our Scientific Advisory Council (SAC), which is made up of leading experts in leukodystrophy and lysosomal storage disorders. Our Research Initiative has awarded more than 72 grants and provided more than $4.7 million in funding since 2002.

Additionally, we support individuals and families to interpret scientific literature and take part in clinical trials and other vital research initiatives.

For information on a specific disease, please visit our Diseases page.

For Individuals
and Families

Learn about ongoing studies and how you can participate in research.

Information for Researchers

Discover grant opportunities, resources, and NTSAD research initiatives.

Clinical Trials

Learn about ongoing studies and how you can participate in research.

Grant Opportunities

Apply for grants for research on Tay-Sachs, Canavan, GM1, and Sandhoff diseases.

Research Priorities

Read more about NTSAD’s efforts in advancing basic and translational research, clinical development, early diagnosis, and newborn screening.