NTSAD Research: Developing Treatments, Therapies, and a Cure
Research to Advance Understanding, Inform Treatment, and Improve Quality of Life
The National Tay-Sachs & Allied Diseases Association (NTSAD) is dedicated to finding effective treatments and – ultimately – a cure for Tay-Sachs, Canavan, GM1, and Sandhoff diseases.
Working with our leadership, we drive research, forge collaboration, and foster community among researchers around the world. NTSAD research is informed by our Scientific Advisory Council (SAC), which is made up of leading experts in leukodystrophyA group of rare genetic disorders that affect the central nervous system by disrupting the growth or maintenance of the myelin sheath that insulates nerve cells. Myelin is commonly referred to as the brain's "white matter", myelin covers nerve cells and ensures the clear transmission of nerve impulses from one part of the body to another. These disorders are progressive, meaning that they tend to get worse throughout the life of the patient. The word leukodystrophy comes from the Greek words leuko (meaning white), trophy (meaning growth), and dys (meaning ill). If you put these words together, the word leukodystrophy describes a set of diseases that affect the growth or maintenance of the white matter (myelin). More and lysosomal storage disorders. Our Research Initiative has awarded more than 65 grants and provided more than $4 million in funding since 2002.
Additionally, we support individuals and families to interpret scientific literature and take part in clinical trials and other vital research initiatives.
For information on a specific disease, please visit our Diseases page.
Learn about ongoing studies and how you can participate in research.
National Tay-Sachs & Allied Diseases Association (NTSAD) leads the worldwide fight to treat and cure Tay-Sachs, Canavan, GM1, and Sandhoff diseases by driving research, forging collaboration, and fostering community. Supporting families is the center of everything we do.
The content of this website is intended for informational purposes only and not intended to be a substitute for professional medical advice, diagnosis, or treatment.
The National Tay-Sachs & Allied Diseases Association (NTSAD) leads the worldwide fight to treat and cure Tay-Sachs, Canavan, GM1, and Sandhoff diseases by driving research, forging collaboration, and fostering community. Supporting families is the center of everything we do.
Get the latest news from NTSAD about our Community, the research that provides hope, and what is happening in the world of rare disease.
2001 Beacon Street, Suite 204
Boston, MA 02135
(617) 277-4463 firstname.lastname@example.org
National Tay-Sachs & Allied Diseases Association
2001 Beacon Street, Suite 204, Boston, MA 02135
(617) 277-4463 | email@example.com